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uniQure BV

Drug Names(s): AMT 130, AMT130

Description: AMT-130 is a gene therapy that utilizes AAV5 viral vector in which miHTT scaffolds are incorporated using uniQure’s baculovirus-based manufacturing platform. The scaffolds are injected into the central nervous system (CNS) to silence the Huntingtin gene (HTT).

AMT-130 News

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